An Interactive Workshop to Improve the Journey to Adulthood in Spinal Muscular Atrophy
Historically, patients with the most severe forms of SMA were largely unable to survive into adulthood and those that did often did not continue to see neurologists. However, with the arrival of therapies that can dramatically shift the path of the disease, more and more patients are entering adult care. Unfortunately, as this transition is a new consideration, many clinicians are still learning how to coordinate and manage it appropriately. As such, this program is designed to bring together clinicians from both sides of these transitions to glean clinical pearls from leaders in the space and the established programs at CHOP and the University of Pennsylvania while opening the floor to attendees to voice their own challenges and solutions in this process.
This program is intended for general neurologists, neuromuscular specialists, and any multidisciplinary clinicians (e.g., pediatricians, cardiologists, pulmonologists, orthopedists) and care teams involved in the transition of patients with SMA from pediatric to adult care.
Upon completion of the educational activity, participants should be able to:
- Recognize the evolving presentations of SMA in the treatment era and how they may change as patients age to adequately understand individual needs and establish care plans accordingly
- Discuss the role of FDA-approved SMA therapeutics, as well as their ongoing evaluation in broadening patient populations (e.g., adult, previously treated), in the transition from pediatric to adult care to better coordinate treatment continuity or make appropriate therapeutic adjustments
- Describe effective transition strategies for patients with SMA as they enter adulthood to ensure seamless, comprehensive, and continued care throughout their lifespans
Note: Each section will include group discussion topics and opportunities to troubleshoot your own practice challenges with other SMA treaters
The Current Picture of Pediatric to Adult Transitions in SMA
- The changing natural history of SMA with current therapies
- What happens when transitions go wrong
- Importance and challenges of maintaining therapy into adulthood; proposed solutions by agent
The Pediatric Side of Transitions
- Transition timeline for success
- Key clinical tools and resources to streamline transition readiness and preparedness
- Insight to potential barriers/challenges from both the pediatric and adult lens; proposed solutions
The Adult Side of Transitions
- Key differences between pediatric and adult care
- How to help a patient with SMA adapt to an adult care model
- Navigating medical, logistical, and social obstacles
Registered attendees will have access to the Mütter Museum Exhibits for one hour at the conclusion of the presentation.
Valet Parking has been arranged for registered attendees, please park in the lot behind the museum at 26 S 21st Street Philadelphia, PA 19103.
This activity is jointly provided by Medical Education Resources (MER) and Efficient LLC.
In support of improving patient care, this activity has been planned and implemented by Medical Education Resources (MER) and Efficient LLC. MER is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.
Disclosure of Relevant Financial Relationships
Medical Education Resources ensures balance, independence, objectivity, and scientific rigor in all our educational activities. In accordance with this policy, MER identifies relevant financial relationships with its instructors, content managers, and other individuals who are in a position to control the content of an activity. Reported relevant financial relationships are mitigated by MER to ensure that all scientific research referred to, reported, or used in a CE activity conforms to the generally accepted standards of experimental design, data collection, and analysis. MER is committed to providing learners with high-quality CE activities that promote improvements or quality in health care and not the business interest of an ineligible company.
Planners' and Managers' Disclosure
Efficient LLC and Medical Education Resources' planners and managers have no financial relationships to disclose.
Dr Brandsema reported the following financial relationships:
- Consulting Fees: Argenx, AveXis/Novartis, Biogen, Fibrogen, Genentech, Momenta/Janssen, NS Pharma, Pfizer, PTC Therapeutics, Sarepta, Scholar Rock
- Grants/Research Support: Alexion, Argenx, Astellas, AveXis/Novartis, Biogen, CSL Behring, Fibrogen, Genentech, Momenta/Janssen, Pfizer, PTC Therapeutics, Sarepta
Dr Elman reported the following financial relationships:
- Consulting Fees: Biogen, Genentech, Edgewise
Disclosure of Unlabeled Use/Disclaimer
This educational activity may contain discussion of published and/or investigational uses of agents that are not indicated by the FDA. The planners of this activity do not recommend the use of any agent outside of the labeled indications. The opinions expressed in the educational activity are those of the faculty and do not necessarily represent the views of the planners. Please refer to the official prescribing information for each product for discussion of approved indications, contraindications, and warnings.
The content and views presented in this educational activity are those of the authors and do not necessarily reflect those of Medical Education Resources, Efficient LLC, and/or Genentech. The authors have disclosed if there is any discussion of published and/or investigational uses of agents that are not indicated by the FDA in their presentations. Before prescribing any medicine, primary references and full prescribing information should be consulted. Any procedures, medications, or other courses of diagnosis or treatment discussed or suggested in this activity should not be used by clinicians without evaluation of their patient’s conditions and possible contraindications on dangers in use, review of any applicable manufacturer’s product information, and comparison with recommendations of other authorities. The information presented in this activity is not meant to serve as a guideline for patient management.
This continuing education activity is supported by an educational grant from Genentech, a member of the Roche group.